title: Patient organizations and research on rare diseases.
authors.forename: Julie R
authors.initials: JR
authors.lastname: Ingelfinger
authors.forename: Jeffrey M
authors.initials: JM
authors.lastname: Drazen
mesh_terms: D005260:Female; D005582:Foundations; D006801:Humans; D018192:Lymphangioleiomyomatosis / Q000188:drug therapy*; D035583:Rare Diseases; D012657:Self-Help Groups; D020123:Sirolimus / Q000627:therapeutic use*; D058570:TOR Serine-Threonine Kinases / Q000037:antagonists & inhibitors
chemical_list: C546842:MTOR protein, human; D058570:TOR Serine-Threonine Kinases; D020123:Sirolimus