title: Orphan cystic fibrosis drugs find sister diseases.
authors.forename: Elie
authors.initials: E
authors.lastname: Dolgin
mesh_terms: D000627:Aminophenols / Q000627:therapeutic use; D003550:Cystic Fibrosis / Q000188:drug therapy* / Q000235:genetics; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000819:agonists / Q000037:antagonists & inhibitors / Q000235:genetics; D055808:Drug Discovery; D006801:Humans; D050505:Mutant Proteins / Q000819:agonists / Q000037:antagonists & inhibitors / Q000235:genetics; D009965:Orphan Drug Production; D015363:Quinolones / Q000627:therapeutic use
chemical_list: D000627:Aminophenols; C505032:CFTR protein, human; D050505:Mutant Proteins; D015363:Quinolones; D019005:Cystic Fibrosis Transmembrane Conductance Regulator; C545203:ivacaftor