title: Exon-skipping therapy for Duchenne muscular dystrophy.
authors.affiliation: Department of Medicine (Neurology and Rheumatology), Shinshu University School of Medicine, Matsumoto 390-8621, Japan. anakamu@shinshu-u.ac.jp
authors.forename: Akinori
authors.initials: A
authors.lastname: Nakamura
authors.forename: Shin'ichi
authors.initials: S
authors.lastname: Takeda
mesh_terms: D016189:Dystrophin / Q000235:genetics / Q000378:metabolism; D005091:Exons / Q000235:genetics*; D006801:Humans; D008297:Male; D009025:Morpholines / Q000627:therapeutic use*; D060172:Morpholinos; D018482:Muscle, Skeletal / Q000378:metabolism; D020388:Muscular Dystrophy, Duchenne / Q000188:drug therapy* / Q000235:genetics / Q000378:metabolism; D009841:Oligonucleotides / Q000627:therapeutic use*; D016366:Open Reading Frames / Q000187:drug effects / Q000235:genetics
chemical_list: D016189:Dystrophin; D009025:Morpholines; D060172:Morpholinos; D009841:Oligonucleotides; C000611335:eteplirsen