title: [Gene therapy starts to tackle CNS disease].
authors.affiliation: Department of Pediatric Neurology, Hôpital Saint-Vincent de Paul, Paris, France.
authors.forename: Patrick
authors.initials: P
authors.lastname: Aubourg
mesh_terms: D000074063:ATP Binding Cassette Transporter, Subfamily D, Member 1; D018528:ATP-Binding Cassette Transporters / Q000235:genetics; D000326:Adrenoleukodystrophy / Q000235:genetics / Q000628:therapy*; D002493:Central Nervous System Diseases / Q000628:therapy*; D002648:Child; D005260:Female; D015316:Genetic Therapy; D005822:Genetic Vectors; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D016086:Lentivirus; D008297:Male; D014184:Transplantation, Homologous
chemical_list: C115572:ABCD1 protein, human; D000074063:ATP Binding Cassette Transporter, Subfamily D, Member 1; D018528:ATP-Binding Cassette Transporters