title: Gene therapy restores missing cone-mediated vision in the CNGA3-/- mouse model of achromatopsia.
authors.affiliation: Department of Pharmacy, Center for Integrated Protein Science Munich (CIPSM), Center for Drug Research, Ludwig-Maximilians-Universität München, Munich, Germany.
authors.forename: Stylianos
authors.initials: S
authors.lastname: Michalakis
authors.forename: Regine
authors.initials: R
authors.lastname: Mühlfriedel
authors.forename: Naoyuki
authors.initials: N
authors.lastname: Tanimoto
authors.forename: Vidhyasankar
authors.initials: V
authors.lastname: Krishnamoorthy
authors.forename: Susanne
authors.initials: S
authors.lastname: Koch
authors.forename: M Dominik
authors.initials: MD
authors.lastname: Fischer
authors.forename: Elvir
authors.initials: E
authors.lastname: Becirovic
authors.forename: Lin
authors.initials: L
authors.lastname: Bai
authors.forename: Gesine
authors.initials: G
authors.lastname: Huber
authors.forename: Susanne C
authors.initials: SC
authors.lastname: Beck
authors.forename: Edda
authors.initials: E
authors.lastname: Fahl
authors.forename: Hildegard
authors.initials: H
authors.lastname: Büning
authors.forename: Jennifer
authors.initials: J
authors.lastname: Schmidt
authors.forename: Xiangang
authors.initials: X
authors.lastname: Zong
authors.forename: Tim
authors.initials: T
authors.lastname: Gollisch
authors.forename: Martin
authors.initials: M
authors.lastname: Biel
authors.forename: Mathias W
authors.initials: MW
authors.lastname: Seeliger
mesh_terms: D000818:Animals; D055253:Color Vision / Q000235:genetics; D003117:Color Vision Defects / Q000235:genetics* / Q000628:therapy*; D054815:Cyclic Nucleotide-Gated Cation Channels / Q000235:genetics*; D000229:Dependovirus / Q000235:genetics; D004596:Electroretinography; D015316:Genetic Therapy / Q000379:methods*; D057809:HEK293 Cells; D006801:Humans; D051379:Mice; D011994:Recombinant Proteins / Q000235:genetics; D020127:Recovery of Function / Q000235:genetics; D017949:Retinal Cone Photoreceptor Cells / Q000502:physiology*; D017948:Retinal Rod Photoreceptor Cells / Q000502:physiology
chemical_list: C518237:Cnga3 protein, mouse; D054815:Cyclic Nucleotide-Gated Cation Channels; D011994:Recombinant Proteins