title: Gene therapy for Fanconi anemia: one step closer to the clinic.
authors.affiliation: Division of Blood and Marrow Transplantation, University of Minnesota , Minneapolis, MN 55455, USA. tolar003@umn.edu
authors.forename: Jakub
authors.initials: J
authors.lastname: Tolar
authors.forename: Pamela S
authors.initials: PS
authors.lastname: Becker
authors.forename: D Wade
authors.initials: DW
authors.lastname: Clapp
authors.forename: Helmut
authors.initials: H
authors.lastname: Hanenberg
authors.forename: Cristina Díaz
authors.initials: CD
authors.lastname: de Heredia
authors.forename: Hans-Peter
authors.initials: HP
authors.lastname: Kiem
authors.forename: Susana
authors.initials: S
authors.lastname: Navarro
authors.forename: Pankaj
authors.initials: P
authors.lastname: Qasba
authors.forename: Paula
authors.initials: P
authors.lastname: Rio
authors.forename: Manfred
authors.initials: M
authors.lastname: Schmidt
authors.forename: Julián
authors.initials: J
authors.lastname: Sevilla
authors.forename: Els
authors.initials: E
authors.lastname: Verhoeyen
authors.forename: Adrian J
authors.initials: AJ
authors.lastname: Thrasher
authors.forename: Juan
authors.initials: J
authors.lastname: Bueren
mesh_terms: D000818:Animals; D002986:Clinical Trials as Topic; D004249:DNA Damage; D005199:Fanconi Anemia / Q000503:physiopathology / Q000628:therapy*; D052217:Fanconi Anemia Complementation Group A Protein / Q000235:genetics*; D015316:Genetic Therapy / Q000009:adverse effects / Q000379:methods* / Q000639:trends; D006801:Humans
chemical_list: C498471:FANCA protein, human; D052217:Fanconi Anemia Complementation Group A Protein