title: Sense in antisense therapy for spinal muscular atrophy.
authors.affiliation: Children's Hospital of Eastern Ontario and the University of Ottawa, Ottawa.
authors.forename: Alex
authors.initials: A
authors.lastname: MacKenzie
mesh_terms: D017398:Alternative Splicing; D000818:Animals; D015316:Genetic Therapy; D006801:Humans; D051379:Mice; D009046:Motor Neurons / Q000187:drug effects; D009134:Muscular Atrophy, Spinal / Q000235:genetics / Q000628:therapy*; D016376:Oligonucleotides, Antisense / Q000627:therapeutic use*; D012333:RNA, Messenger; D055540:Survival of Motor Neuron 2 Protein / Q000235:genetics*
chemical_list: D016376:Oligonucleotides, Antisense; D012333:RNA, Messenger; D055540:Survival of Motor Neuron 2 Protein