title: [Why does knowledge on rare diseases allow progress in treatments?].
authors.forename: Constance Barazzone
authors.initials: CB
authors.lastname: Argiroffo
authors.forename: A
authors.initials: A
authors.lastname: Superti-Furga
mesh_terms: D035843:Biomedical Research; D002648:Child; D006801:Humans; D035583:Rare Diseases / Q000628:therapy*