title: Gene therapy for retinal dystrophies: twenty years in the making.
authors.affiliation: Department of Genetics, University College London Institute of Ophthalmology, London EC1V 9EL, United Kingdom. r.ali@ucl.ac.uk
authors.forename: Robin R
authors.initials: RR
authors.lastname: Ali
mesh_terms: D000818:Animals; D000229:Dependovirus / Q000235:genetics*; D003911:Dextrans / Q000737:chemistry*; D005136:Eye Proteins / Q000235:genetics*; D015316:Genetic Therapy / Q000379:methods*; D005989:Glycerides / Q000737:chemistry*; D006801:Humans; D008565:Membrane Proteins / Q000235:genetics*; D009154:Mutation; D053758:Nanoparticles; D011479:Protamines / Q000737:chemistry*; D012313:RNA / Q000235:genetics*; D012160:Retina / Q000473:pathology* / Q000503:physiopathology*; D012174:Retinitis Pigmentosa / Q000628:therapy*; D041441:Retinoschisis / Q000628:therapy*; D012243:Rhodopsin / Q000235:genetics*; D000099274:Frizzled-Related Proteins
chemical_list: D003911:Dextrans; D005136:Eye Proteins; D005989:Glycerides; D008565:Membrane Proteins; D011479:Protamines; D012313:RNA; D012243:Rhodopsin; C490110:MFRP protein, human; D000099274:Frizzled-Related Proteins; C423368:Mfrp protein, mouse