Platelet-directed gene therapy overcomes inhibitory antibodies to factor VIII.
Department of Gene Therapy and Regenerative Medicine, Free University of Brussels (VUB), Brussels, Belgium.
M K
MK
Chuah
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T
Vandendriessche
D000818:Animals; D001323:Autoantibodies / Q000097:blood*; D001792:Blood Platelets / Q000378:metabolism*; D016026:Bone Marrow Transplantation; D005169:Factor VIII / Q000378:metabolism*; D015316:Genetic Therapy; D005822:Genetic Vectors; D018380:Hematopoietic Stem Cell Transplantation; D006467:Hemophilia A / Q000628:therapy*; D016086:Lentivirus / Q000235:genetics*
D001323:Autoantibodies; D005169:Factor VIII