Challenges in vector and trial design using retroviral vectors for long-term gene correction in hematopoietic stem cell gene therapy.
Biotechnology Activities, National Institutes of Health, Bethesda, Maryland, USA.
Jacqueline
J
Corrigan-Curay
Odile
O
Cohen-Haguenauer
Marina
M
O'Reilly
Susan R
SR
Ross
Hung
H
Fan
Naomi
N
Rosenberg
Nikunj
N
Somia
Nancy
N
King
Theodore
T
Friedmann
Cynthia
C
Dunbar
Alessandro
A
Aiuti
Luigi
L
Naldini
Christopher
C
Baum
Christof
C
von Kalle
Hans-Peter
HP
Kiem
Eugenio
E
Montini
Frederic
F
Bushman
Brian P
BP
Sorrentino
Manuel
M
Carrondo
Harry
H
Malech
Gösta
G
Gahrton
Robyn
R
Shapiro
Linda
L
Wolff
Eugene
E
Rosenthal
Robert
R
Jambou
John
J
Zaia
Donald B
DB
Kohn
D018014:Gene Transfer Techniques; D015316:Genetic Therapy / Q000009:adverse effects / Q000941:ethics / Q000331:legislation & jurisprudence; D005822:Genetic Vectors / Q000009:adverse effects / Q000235:genetics; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D012107:Research Design; D012190:Retroviridae / Q000235:genetics*