title: Eltrombopag fails to improve severe thrombocytopenia in late-stage dyskeratosis congenita and diamond-blackfan-anaemia.
authors: Karolin
authors: K
authors: Trautmann
authors: Christiane
authors: C
authors: Jakob
authors: Ulrich
authors: U
authors: von Grünhagen
authors: Eberhard
authors: E
authors: Schleyer
authors: Tim H
authors: TH
authors: Brümmendorf
authors: Gabriele
authors: G
authors: Siegert
authors: Gerhard
authors: G
authors: Ehninger
authors: Uwe
authors: U
authors: Platzbecker
mesh_terms: D000284:Administration, Oral; D000293:Adolescent; D000328:Adult; D029503:Anemia, Diamond-Blackfan / Q000188:drug therapy* / Q000235:genetics; D001565:Benzoates / Q000627:therapeutic use*; D002309:Cardiology / Q000379:methods; D019871:Dyskeratosis Congenita / Q000188:drug therapy* / Q000235:genetics; D005260:Female; D006801:Humans; D006834:Hydrazines / Q000627:therapeutic use*; D008297:Male; D008533:Megakaryocytes / Q000166:cytology; D011720:Pyrazoles / Q000627:therapeutic use*; D053628:Receptors, Thrombopoietin / Q000819:agonists; D013921:Thrombocytopenia / Q000188:drug therapy* / Q000209:etiology; D016896:Treatment Outcome
chemical_list: D001565:Benzoates; D006834:Hydrazines; D011720:Pyrazoles; D053628:Receptors, Thrombopoietin; C520809:eltrombopag