title: Gene therapy through autologous transplantation of gene-modified hematopoietic stem cells.
authors.affiliation: Department of Microbiology, Immunology, and Molecular Genetics, University of California Los Angeles, Los Angeles, California 90095, USA. dkohn@mednet.ucla.edu
authors.forename: Donald B
authors.initials: DB
authors.lastname: Kohn
authors.forename: Sung-Yun
authors.initials: SY
authors.lastname: Pai
authors.forename: Michel
authors.initials: M
authors.lastname: Sadelain
mesh_terms: D000818:Animals; D030342:Genetic Diseases, Inborn / Q000235:genetics / Q000378:metabolism / Q000628:therapy; D015316:Genetic Therapy / Q000379:methods*; D006402:Hematologic Diseases / Q000235:genetics / Q000378:metabolism / Q000628:therapy; D018380:Hematopoietic Stem Cell Transplantation / Q000379:methods*; D006412:Hematopoietic Stem Cells / Q000378:metabolism; D006801:Humans; D014182:Transplantation, Autologous; D014184:Transplantation, Homologous