title: Alglucosidase alfa and Pompe disease: still going strong?
authors.affiliation: Division of Medical Genetics, Department of Pediatrics, University of Virginia Health System, 1801 Hospital Drive, PO Box 800386, Charlottesville, VA 22908, USA. slipinski@virginia.edu
authors.forename: Shawn E
authors.initials: SE
authors.lastname: Lipinski
mesh_terms: D056947:Enzyme Replacement Therapy; D005260:Female; D006009:Glycogen Storage Disease Type II / Q000188:drug therapy* / Q000473:pathology*; D006801:Humans; D008297:Male; D000520:alpha-Glucosidases / Q000627:therapeutic use*
chemical_list: C509951:GAA protein, human; D000520:alpha-Glucosidases