Rare disease clinical research network's urea cycle consortium delivers a successful clinical trial to improve alternate pathway therapy.
Pramod K
PK
Mistry
D000641:Ammonia / Q000097:blood*; D005260:Female; D005990:Glycerol / Q000031:analogs & derivatives* / Q000627:therapeutic use; D006801:Humans; D008297:Male; D010654:Phenylbutyrates / Q000627:therapeutic use*; D056806:Urea Cycle Disorders, Inborn / Q000188:drug therapy*
D010654:Phenylbutyrates; D000641:Ammonia; C075773:4-phenylbutyric acid; D005990:Glycerol; C570223:glycerol phenylbutyrate