title: Treosulfan-based conditioning in DOCK8 deficiency: complete lympho-hematopoietic reconstitution with minimal toxicity.
authors.forename: Sujal
authors.initials: S
authors.lastname: Ghosh
authors.forename: Friedhelm R
authors.initials: FR
authors.lastname: Schuster
authors.forename: Ilka
authors.initials: I
authors.lastname: Fuchs
authors.forename: Hans-Jürgen
authors.initials: HJ
authors.lastname: Laws
authors.forename: Arndt
authors.initials: A
authors.lastname: Borkhardt
authors.forename: Roland
authors.initials: R
authors.lastname: Meisel
mesh_terms: D002066:Busulfan / Q000031:analogs & derivatives / Q000627:therapeutic use; D002648:Child; D005260:Female; D020662:Guanine Nucleotide Exchange Factors / Q000172:deficiency* / Q000235:genetics; D006410:Hematopoiesis; D006801:Humans; D007589:Job Syndrome / Q000235:genetics / Q000276:immunology / Q000628:therapy*; D036102:Peripheral Blood Stem Cell Transplantation; D013997:Time Factors; D019172:Transplantation Conditioning / Q000009:adverse effects / Q000379:methods*
chemical_list: C516591:DOCK8 protein, human; D020662:Guanine Nucleotide Exchange Factors; C018404:treosulfan; D002066:Busulfan