title: Gene therapy for ADA-SCID: defining the factors for successful outcome.
authors.affiliation: University College London Institute of Child Health.
authors.forename: H Bobby
authors.initials: HB
authors.lastname: Gaspar
mesh_terms: D000243:Adenosine Deaminase / Q000172:deficiency / Q000627:therapeutic use*; D000361:Agammaglobulinemia / Q000628:therapy*; D000818:Animals; D016026:Bone Marrow Transplantation / Q000379:methods*; D005260:Female; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors; D018380:Hematopoietic Stem Cell Transplantation / Q000379:methods*; D006801:Humans; D008297:Male; D016511:Severe Combined Immunodeficiency / Q000628:therapy*; D019172:Transplantation Conditioning / Q000379:methods*
chemical_list: D000243:Adenosine Deaminase