title: Trial watch: enzyme replacement success in Phase III trial for rare metabolic disorder.
authors.forename: Sarah
authors.initials: S
authors.lastname: Crunkhorn
mesh_terms: D002811:Chondroitinsulfatases / Q000627:therapeutic use*; D017326:Clinical Trials, Phase III as Topic; D004345:Drug Industry; D056947:Enzyme Replacement Therapy; D006801:Humans; D009085:Mucopolysaccharidosis IV / Q000188:drug therapy* / Q000201:enzymology
chemical_list: D002811:Chondroitinsulfatases; C102295:GALNS protein, human