title: Transplantation of gene-corrected motor neurons as a therapeutic strategy for spinal muscular atrophy.
authors: Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.
authors: Kathrin
authors: K
authors: Meyer
authors: Carlos J
authors: CJ
authors: Miranda
authors: Brian K
authors: BK
authors: Kaspar
mesh_terms: D000818:Animals; D004195:Disease Models, Animal; D015316:Genetic Therapy / Q000379:methods; D006801:Humans; D051379:Mice; D009046:Motor Neurons / Q000166:cytology / Q000637:transplantation*; D009134:Muscular Atrophy, Spinal / Q000235:genetics* / Q000628:therapy*; D039904:Pluripotent Stem Cells / Q000166:cytology*; D055540:Survival of Motor Neuron 2 Protein / Q000235:genetics
chemical_list: C526477:SMN2 protein, human; D055540:Survival of Motor Neuron 2 Protein