title: Therapy for lysosomal acid lipase deficiency: replacing a missing link.
authors.forename: Gregory
authors.initials: G
authors.lastname: Grabowski
mesh_terms: D015217:Cholesterol Ester Storage Disease / Q000188:drug therapy*; D005260:Female; D006801:Humans; D008297:Male; D011994:Recombinant Proteins / Q000009:adverse effects* / Q000627:therapeutic use*; D002787:Sterol Esterase / Q000009:adverse effects* / Q000627:therapeutic use*
chemical_list: D011994:Recombinant Proteins; D002787:Sterol Esterase