title: From mutation identification to therapy: discovery and origins of the first approved gene therapy in the Western world.
authors.affiliation: Department of Vascular Medicine, Academic Medical Centre, University of Amsterdam, The Netherlands. j.j.kastelein@amc.uva.nl
authors.forename: John J P
authors.initials: JJ
authors.lastname: Kastelein
authors.forename: Colin J D
authors.initials: CJ
authors.lastname: Ross
authors.forename: Michael R
authors.initials: MR
authors.lastname: Hayden
mesh_terms: D015316:Genetic Therapy / Q000266:history*; D049673:History, 20th Century; D006801:Humans; D008072:Hyperlipoproteinemia Type I / Q000235:genetics / Q000628:therapy; D009154:Mutation / Q000235:genetics*; D019366:Western World