title: Splicing: hear and now!
authors: Sarepta Therapeutics, Inc., Cambridge, Massachusetts 02142, USA. RKoleAdvisor@sareptatherapeutics.com
authors: Ryszard
authors: R
authors: Kole
mesh_terms: D000818:Animals; D002352:Carrier Proteins / Q000235:genetics*; D006801:Humans; D016376:Oligonucleotides, Antisense / Q000627:therapeutic use*; D052245:Usher Syndromes / Q000235:genetics* / Q000628:therapy*
chemical_list: D002352:Carrier Proteins; D016376:Oligonucleotides, Antisense
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