title: Regulatory watch: enhanced chance of success for protein replacement therapies.
authors.forename: Sarah
authors.initials: S
authors.lastname: Crunkhorn
mesh_terms: D000818:Animals; D002986:Clinical Trials as Topic / Q000331:legislation & jurisprudence / Q000639:trends; D056947:Enzyme Replacement Therapy / Q000379:methods* / Q000639:trends; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000188:drug therapy* / Q000201:enzymology / Q000378:metabolism*; D009965:Orphan Drug Production / Q000331:legislation & jurisprudence* / Q000379:methods*; D021381:Protein Transport / Q000502:physiology