title: [Exon skipping therapy for Duchenne muscular dystrophy: outcome of preclinical study and prospective for clinical study].
authors.affiliation: anakamu@ncnp.go.jp
authors.forename: A
authors.initials: A
authors.lastname: Nakamura
authors.forename: S
authors.initials: S
authors.lastname: Takeda
mesh_terms: D000818:Animals; D016189:Dystrophin / Q000235:genetics; D005091:Exons / Q000235:genetics*; D006801:Humans; D020388:Muscular Dystrophy, Duchenne / Q000175:diagnosis / Q000235:genetics / Q000473:pathology / Q000628:therapy*; D009154:Mutation / Q000235:genetics*; D011446:Prospective Studies; D016896:Treatment Outcome
chemical_list: D016189:Dystrophin