title: Medicine. Gene therapy that works.
authors: Laboratory of Genetics, The Salk Institute, La Jolla, CA 92037, USA. verma@salk.edu
authors: Inder M
authors: IM
authors: Verma
mesh_terms: D002553:Cerebroside-Sulfatase / Q000235:genetics*; D015316:Genetic Therapy / Q000379:methods*; D018380:Hematopoietic Stem Cell Transplantation; D006412:Hematopoietic Stem Cells / Q000378:metabolism*; D006801:Humans; D007966:Leukodystrophy, Metachromatic / Q000628:therapy*; D008297:Male; D014923:Wiskott-Aldrich Syndrome / Q000628:therapy*; D051316:Wiskott-Aldrich Syndrome Protein / Q000235:genetics*
chemical_list: D051316:Wiskott-Aldrich Syndrome Protein; D002553:Cerebroside-Sulfatase