A commentary on high-dose enzyme replacement therapy attenuates cerebroventriculomegaly in a mouse model of mucopolysaccharidosis type II.
Program for the Study of Neurodevelopment in Rare Disorders, Children's Hospital of Pittsburgh, University of Pittsburgh Medical Center, Pittsburgh, PA, USA.
Maria L
ML
Escolar
D000818:Animals; D001921:Brain / Q000187:drug effects*; D056947:Enzyme Replacement Therapy; D006023:Glycoproteins / Q000627:therapeutic use*; D006801:Humans; D006849:Hydrocephalus / Q000188:drug therapy*; D016532:Mucopolysaccharidosis II / Q000188:drug therapy*
D006023:Glycoproteins