Using induced human pluripotent stem cells to study Diamond-Blackfan anemia: an outlook on the clinical possibilities.
Department of Pediatrics, Comprehensive Bone Marrow Failure Center, Division of Hematology, The Children's Hospital of Philadelphia, Philadelphia, PA 19104, USA.
Philip J
PJ
Mason
Nieves
N
Perdigones
Monica
M
Bessler
D029503:Anemia, Diamond-Blackfan / Q000473:pathology* / Q000601:surgery*; D002454:Cell Differentiation; D064987:Cell- and Tissue-Based Therapy; D015316:Genetic Therapy; D006801:Humans; D039904:Pluripotent Stem Cells / Q000166:cytology / Q000637:transplantation*