title: New targets for old diseases: lessons from mucolipidosis type II.
authors.affiliation: Telethon Institute of Genetics and Medicine (TIGEM), Naples, Italy; Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, USA; Jan and Dan Duncan Neurological Research Institute, Texas Children Hospital, Houston, TX, USA; Department of Translational and Medical Sciences, Medical Genetics, Federico II University, Naples, Italy.
authors.forename: Carmine
authors.initials: C
authors.lastname: Settembre
authors.forename: Andrea
authors.initials: A
authors.lastname: Ballabio
mesh_terms: D000818:Animals; D001846:Bone Development; D005260:Female; D006801:Humans; D009081:Mucolipidoses / Q000473:pathology*; D010010:Osteoclasts / Q000378:metabolism*
keywords: lysosomal storage disorders; lysosome; osteoblast; osteoclast; skeleton