Gene therapy arrives at the macula.
Wilmer Eye Institute, Johns Hopkins University School of Medicine, Baltimore, MD 21287-9277, USA. Electronic address: hscholl1@jhmi.edu.
Hendrik P N
HP
Scholl
INSERM, U968, Institut de la Vision, Paris, France; Sorbonne Universités, UPMC University Paris 06, UMR S968, Institut de la Vision, Paris, France; CNRS, UMR 7210, Institut de la Vision, Paris, France; Fondation Ophtalmologique Adolphe de Rothschild, Paris, France; CIC-1423, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Paris, France; Institute of Ophthalmology, University College of London, London, UK.
José A
JA
Sahel
D048868:Adaptor Proteins, Signal Transducing / Q000008:administration & dosage*; D015794:Choroideremia / Q000628:therapy*; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors / Q000008:administration & dosage*; D006801:Humans; D008297:Male
D048868:Adaptor Proteins, Signal Transducing; C081787:CHM protein, human