Treatment of erythropoietic protoporphyria with the oral sorbent colestipol: a proof-of-concept clinical trial.
Division of Genetics, Brigham and Women's Hospital and Harvard Medical School, Boston, Massachusetts; Channing Division of Network Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, Massachusetts. Electronic address: peter.tishler@channing.harvard.edu.
Peter V
PV
Tishler
Channing Division of Network Medicine, Brigham and Women's Hospital and Harvard Medical School, Boston, Massachusetts.
Bernard
B
Rosner
D000284:Administration, Oral; D000328:Adult; D000837:Anion Exchange Resins / Q000008:administration & dosage*; D003084:Colestipol / Q000008:administration & dosage*; D004305:Dose-Response Relationship, Drug; D004334:Drug Administration Schedule; D005260:Female; D005500:Follow-Up Studies; D006801:Humans; D046351:Protoporphyria, Erythropoietic / Q000175:diagnosis / Q000188:drug therapy*; D012720:Severity of Illness Index; D013997:Time Factors; D016896:Treatment Outcome
D000837:Anion Exchange Resins; D003084:Colestipol