title: Optimizing treatments in rare diseases: will our evidence come from registry data?
authors.affiliation: Serviço de Hematologia, Instituto Português de Oncologia de Lisboa, Francisco Gentil, Lisbon, Portugal. Electronic address: amalmeida@ipolisboa.min-saude.pt.
authors.forename: Antonio M
authors.initials: AM
authors.lastname: Almeida
mesh_terms: D000964:Antimetabolites, Antineoplastic / Q000627:therapeutic use*; D001374:Azacitidine / Q000627:therapeutic use*; D005260:Female; D006801:Humans; D015477:Leukemia, Myelomonocytic, Chronic / Q000188:drug therapy* / Q000401:mortality*; D008297:Male
chemical_list: D000964:Antimetabolites, Antineoplastic; D001374:Azacitidine