title: An Orphan Drug Framework (ODF) for Canada.
abstract: An orphan drug is a pharmaceutical or biological drug that is used to treat a rare disease. The development of a Canadian orphan drug framework is intended to help translate scientific discoveries into meaningful results for Canadian rare disease patients.
authors.forename: David K
authors.initials: DK
authors.lastname: Lee
authors.forename: Barbara
authors.initials: B
authors.lastname: Wong
mesh_terms: D002170:Canada; D006801:Humans; D009965:Orphan Drug Production / Q000331:legislation & jurisprudence*; D035583:Rare Diseases / Q000188:drug therapy*