title: [The telethon and the promises not kept by gene therapy].
authors.forename: Jean-Yves
authors.initials: JY
authors.lastname: Nau
mesh_terms: D005653:Fund Raising; D015316:Genetic Therapy; D006801:Humans; D009468:Neuromuscular Diseases / Q000235:genetics / Q000628:therapy; D035583:Rare Diseases / Q000235:genetics / Q000628:therapy; D012106:Research