Dystrophin as a therapeutic biomarker: are we ignoring data from the past?
Western Australian Neuroscience Research Institute and Centre for Comparative Genomics, Murdoch University, Murdoch, Western Australia, Australia. Electronic address: steve.wilton@uwa.edu.au.
Steve D
SD
Wilton
Western Australian Neuroscience Research Institute and Centre for Comparative Genomics, Murdoch University, Murdoch, Western Australia, Australia.
Sue
S
Fletcher
Center for Gene Therapy, The Research Institute, Nationwide Children's Hospital, Columbus, OH, USA.
Kevin M
KM
Flanigan
D015415:Biomarkers; D016189:Dystrophin / Q000235:genetics* / Q000378:metabolism; D006801:Humans; D008297:Male; D020388:Muscular Dystrophy, Duchenne / Q000235:genetics* / Q000378:metabolism / Q000628:therapy
D015415:Biomarkers; D016189:Dystrophin
Biomarker; Duchenne muscular dystrophy; Dystrophin; Exon skipping