title: Does the orphan medicinal product regulation assist or hinder access to innovative haemophilia treatment in Europe?
authors.affiliation: European Haemophilia Consortium, Brussels, Belgium; Irish Haemophilia Society, Haemophilia Product Selection Monitoring and Advisory Board, Ireland.
authors.forename: B
authors.initials: B
authors.lastname: O'Mahony
authors.forename: F
authors.initials: F
authors.lastname: Peyvandi
authors.forename: A
authors.initials: A
authors.lastname: Bok
mesh_terms: D005060:Europe; D006467:Hemophilia A / Q000188:drug therapy*; D006801:Humans; D062069:Inventions; D040541:Marketing; D009965:Orphan Drug Production / Q000191:economics; D012926:Social Control, Formal