title: Research into rare diseases of childhood.
authors.affiliation: Children's National Medical Center, Washington, DC.
authors.forename: Mark L
authors.initials: ML
authors.lastname: Batshaw
authors.affiliation: Office of Rare Diseases Research, National Center for Advancing Translational Sciences, National Institutes of Health, Bethesda, Maryland.
authors.forename: Stephen C
authors.initials: SC
authors.lastname: Groft
authors.affiliation: Pediatric Epidemiology Center, University of South Florida, Tampa.
authors.forename: Jeffrey P
authors.initials: JP
authors.lastname: Krischer
mesh_terms: D035843:Biomedical Research / Q000458:organization & administration / Q000639:trends*; D002648:Child; D002986:Clinical Trials as Topic; D006801:Humans; D007878:Legislation as Topic; D009965:Orphan Drug Production; D035583:Rare Diseases; D014481:United States