Targeting nonsense-mediated cystic fibrosis: is it premature to stop now?
University of Massachusetts Medical School, Worcester, MA 01655, USA. Electronic address: osullivb@ummhc.org.
Brian P
BP
O'Sullivan
D003550:Cystic Fibrosis / Q000188:drug therapy* / Q000235:genetics*; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000235:genetics*; D005260:Female; D006801:Humans; D008297:Male; D010069:Oxadiazoles / Q000627:therapeutic use*
C505032:CFTR protein, human; D010069:Oxadiazoles; D019005:Cystic Fibrosis Transmembrane Conductance Regulator; C515878:ataluren