title: Therapeutic challenge in leukodystrophies: translational and ethical research toward clinical trials (LeukoTreat).
mesh_terms: D064987:Cell- and Tissue-Based Therapy; D002553:Cerebroside-Sulfatase / Q000235:genetics / Q000378:metabolism; D032984:Ethics, Research; D005698:Galactosylceramidase / Q000235:genetics / Q000378:metabolism; D015316:Genetic Therapy; D005822:Genetic Vectors / Q000235:genetics / Q000378:metabolism; D018380:Hematopoietic Stem Cell Transplantation; D006412:Hematopoietic Stem Cells / Q000166:cytology / Q000378:metabolism; D020279:Hereditary Central Nervous System Demyelinating Diseases / Q000628:therapy*; D006801:Humans
chemical_list: D002553:Cerebroside-Sulfatase; D005698:Galactosylceramidase