title: Augmenting PBGD expression in the liver as a novel gene therapy for acute intermittent porphyria (AIPgene).
mesh_terms: D000818:Animals; D000229:Dependovirus / Q000235:genetics; D004195:Disease Models, Animal; D015316:Genetic Therapy; D005822:Genetic Vectors / Q000235:genetics / Q000378:metabolism; D011163:Hydroxymethylbilane Synthase / Q000235:genetics* / Q000378:metabolism; D008099:Liver / Q000378:metabolism*; D017118:Porphyria, Acute Intermittent / Q000628:therapy*
chemical_list: D011163:Hydroxymethylbilane Synthase