title: Rare diseases in children: towards better and fairer treatment.
mesh_terms: D002648:Child; D055808:Drug Discovery / Q000191:economics; D006801:Humans; D010372:Pediatrics; D035583:Rare Diseases / Q000188:drug therapy* / Q000191:economics; D057170:Translational Research, Biomedical / Q000379:methods*; D014481:United States; D014486:United States Food and Drug Administration