title: Realizing the potential of patient organizations in translational research-delivering treatments for rare diseases.
authors.affiliation: Scientific Affairs, Association of American Medical Colleges Perelman School of Medicine at the University of Pennsylvania.
authors.forename: Anne C
authors.initials: AC
authors.lastname: Berlin
authors.forename: Elliott R
authors.initials: ER
authors.lastname: Eggan
mesh_terms: D006801:Humans; D009936:Organizational Innovation; D018579:Patient Selection; D035583:Rare Diseases / Q000628:therapy*; D057170:Translational Research, Biomedical / Q000458:organization & administration*; D014481:United States