title: Genotype-based treatment approved for type 1 Gaucher disease.
authors.forename: Cheryl A
authors.initials: CA
authors.lastname: Thompson
mesh_terms: D000328:Adult; D017277:Drug Approval; D004791:Enzyme Inhibitors / Q000494:pharmacology / Q000627:therapeutic use*; D005776:Gaucher Disease / Q000188:drug therapy* / Q000235:genetics; D005838:Genotype; D006801:Humans; D011759:Pyrrolidines / Q000494:pharmacology / Q000627:therapeutic use*; D014481:United States; D014486:United States Food and Drug Administration
chemical_list: D004791:Enzyme Inhibitors; D011759:Pyrrolidines; C522917:eliglustat