title: Phase I/II study of intrapleural administration of a serotype rh.10 replication-deficient adeno-associated virus gene transfer vector expressing the human α1-antitrypsin cDNA to individuals with α1-antitrypsin deficiency.
authors.affiliation: Department of Genetic Medicine, Weill Cornell Medical College , New York, NY 10065.
authors.forename: Maria J
authors.initials: MJ
authors.lastname: Chiuchiolo
authors.forename: Stephen M
authors.initials: SM
authors.lastname: Kaminsky
authors.forename: Dolan
authors.initials: D
authors.lastname: Sondhi
authors.forename: Denesy
authors.initials: D
authors.lastname: Mancenido
authors.forename: Charleen
authors.initials: C
authors.lastname: Hollmann
authors.forename: Ronald G
authors.initials: RG
authors.lastname: Crystal
mesh_terms: D015331:Cohort Studies; D018076:DNA, Complementary / Q000235:genetics / Q000378:metabolism; D000229:Dependovirus / Q000235:genetics*; D005260:Female; D005500:Follow-Up Studies; D018014:Gene Transfer Techniques; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors / Q000235:genetics*; D006801:Humans; D008297:Male; D065288:Serogroup; D000515:alpha 1-Antitrypsin / Q000235:genetics* / Q000378:metabolism; D019896:alpha 1-Antitrypsin Deficiency / Q000628:therapy*
chemical_list: D018076:DNA, Complementary; D000515:alpha 1-Antitrypsin