title: Familial amyloidosis: great progress for an orphan disease.
authors.affiliation: Department of Internal Medicine I, Universitätsmedizin of the Johannes Gutenberg-University Mainz, Germany; Department of Internal Medicine I, Universitätsklinikum of the University Regensburg, Germany. Electronic address: Ana.Barreiros@ukr.de.
authors.forename: Ana Paula
authors.initials: AP
authors.lastname: Barreiros
authors.affiliation: Department of Hepatobiliary and Transplantation Surgery, Universitätsmedizin of the Johannes Gutenberg-University Mainz, Germany.
authors.forename: Gerd
authors.initials: G
authors.lastname: Otto
authors.affiliation: Department of Internal Medicine I, Universitätsmedizin of the Johannes Gutenberg-University Mainz, Germany.
authors.forename: Bita
authors.initials: B
authors.lastname: Kahlen
authors.affiliation: Department of Internal Medicine I, Universitätsmedizin of the Johannes Gutenberg-University Mainz, Germany; Department of Internal Medicine I, Universitätsklinikum of the University Regensburg, Germany.
authors.forename: Andreas
authors.initials: A
authors.lastname: Teufel
authors.affiliation: Department of Internal Medicine I, Universitätsmedizin of the Johannes Gutenberg-University Mainz, Germany.
authors.forename: Peter R
authors.initials: PR
authors.lastname: Galle
mesh_terms: D028226:Amyloidosis, Familial / Q000175:diagnosis / Q000453:epidemiology / Q000628:therapy; D019468:Disease Management; D014943:Global Health; D006801:Humans; D009017:Morbidity; D035583:Rare Diseases
keywords: Familial amyloidosis; Liver transplantation; Pharmacological therapy; Tafamidis