title: Measuring clinical effectiveness of medicinal products for the treatment of Duchenne muscular dystrophy.
authors.affiliation: Newcastle University, Newcastle upon Tyne, UK.
authors.forename: Stephen
authors.initials: S
authors.lastname: Lynn
authors.affiliation: Newcastle University, Newcastle upon Tyne, UK; Leiden University Medical Centre, Leiden, The Netherlands.
authors.forename: Annemieke
authors.initials: A
authors.lastname: Aartsma-Rus
authors.affiliation: Newcastle University, Newcastle upon Tyne, UK.
authors.forename: Kate
authors.initials: K
authors.lastname: Bushby
authors.affiliation: Parent Project Muscular Dystrophy, Hackensack, NJ, USA.
authors.forename: Pat
authors.initials: P
authors.lastname: Furlong
authors.affiliation: University of Leuven, Leuven, Belgium.
authors.forename: Nathalie
authors.initials: N
authors.lastname: Goemans
authors.affiliation: University of Bari, Bari, Italy.
authors.forename: Annamaria
authors.initials: A
authors.lastname: De Luca
authors.affiliation: Newcastle University, Newcastle upon Tyne, UK.
authors.forename: Anna
authors.initials: A
authors.lastname: Mayhew
authors.affiliation: University of California Davis, Davis, CA, USA.
authors.forename: Craig
authors.initials: C
authors.lastname: McDonald
authors.affiliation: Catholic University Rome, Rome, Italy.
authors.forename: Eugenio
authors.initials: E
authors.lastname: Mercuri
authors.affiliation: University College London, London, UK.
authors.forename: Francesco
authors.initials: F
authors.lastname: Muntoni
authors.affiliation: Muscular Dystrophy Campaign, London, UK.
authors.forename: Marita
authors.initials: M
authors.lastname: Pohlschmidt
authors.affiliation: Leiden University Medical Centre, Leiden, The Netherlands.
authors.forename: Jan
authors.initials: J
authors.lastname: Verschuuren
authors.affiliation: University Pierre et Marie Curie Paris 6, Institut de Myologie, UPMC-INSERM UMR 974, CNRS FRE 3617, GH Pitié-Salpêtrière, Paris, France.
authors.forename: Thomas
authors.initials: T
authors.lastname: Voit
authors.affiliation: Duchenne Parent Project, Amsterdam, The Netherlands.
authors.forename: Elizabeth
authors.initials: E
authors.lastname: Vroom
authors.affiliation: Royal Veterinary College, London, UK.
authors.forename: Dominic J
authors.initials: DJ
authors.lastname: Wells
authors.affiliation: Newcastle University, Newcastle upon Tyne, UK. Electronic address: volker.straub@ncl.ac.uk.
authors.forename: Volker
authors.initials: V
authors.lastname: Straub
mesh_terms: D000818:Animals; D002986:Clinical Trials as Topic; D004195:Disease Models, Animal; D006801:Humans; D020388:Muscular Dystrophy, Duchenne / Q000628:therapy*; D010043:Outcome and Process Assessment, Health Care; D016896:Treatment Outcome