title: Long-term outcomes in MPS-IH: throwing stars.
abstract: After a herculean data-gathering effort, in this issue of Blood, Aldenhoven and colleagues from Europe and North America provide an eye-opening assessment of long-term neurocognitive, organ, joint, and tissue function after allogeneic transplantation of children with mucopolysaccharidosis type I–Hurler syndrome (MPS-IH), along with an analysis defining a path to better these outcomes.
authors: HUNTSMAN CANCER INSTITUTE; UNIVERSITY OF UTAH SCHOOL OF MEDICINE; PRIMARY CHILDREN'S HOSPITAL.
authors: Michael A
authors: http://orcid.org/0000-0003-3030-8420
authors: MA
authors: Pulsipher
mesh_terms: D005260:Female; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D008297:Male; D008059:Mucopolysaccharidosis I / Q000628:therapy*