title: Treating genetic disease: Expanding the options.
authors.affiliation: Institute of Liver Studies Division of Transplantation Immunology and Mucosal Biology, King's College London, London, UK.|Pediatric Liver, GI and Nutrition Center, King's College Hospital, London, UK.
authors.forename: Richard J
authors.initials: RJ
authors.lastname: Thompson
authors.affiliation: Liver Center Laboratory Department of Medicine, University of California San Francisco, San Francisco, CA.|Institute for Human Genetics, University of California San Francisco, San Francisco, CA.
authors.forename: Laura N
authors.initials: LN
authors.lastname: Bull
mesh_terms: D018528:ATP-Binding Cassette Transporters / Q000187:drug effects*; D000818:Animals; D002780:Cholestasis, Intrahepatic / Q000188:drug therapy*; D005260:Female; D006801:Humans; D008297:Male; D058990:Molecular Targeted Therapy / Q000379:methods*; D010654:Phenylbutyrates / Q000627:therapeutic use*
chemical_list: D018528:ATP-Binding Cassette Transporters; D010654:Phenylbutyrates