title: A shot in the bone corrects a genetic disease.
authors: Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York USA.
authors: Brian D
authors: BD
authors: Brown
mesh_terms: D000818:Animals; D001792:Blood Platelets / Q000378:metabolism*; D005169:Factor VIII / Q000235:genetics*; D005822:Genetic Vectors / Q000008:administration & dosage*; D006467:Hemophilia A / Q000628:therapy*; D006801:Humans; D016086:Lentivirus / Q000235:genetics*
chemical_list: D005169:Factor VIII