title: Fighting rare diseases: the model of the telethon research institutes in Italy.
authors.affiliation: 1 Telethon Institute of Genetics and Medicine (TIGEM) , Pozzuoli, Naples 80078, Italy .
authors.forename: Andrea
authors.initials: A
authors.lastname: Ballabio
authors.forename: Luigi
authors.initials: L
authors.lastname: Naldini
mesh_terms: D000047:Academies and Institutes / Q000458:organization & administration*; D000818:Animals; D030342:Genetic Diseases, Inborn / Q000235:genetics* / Q000628:therapy; D036281:Genetic Research; D015316:Genetic Therapy; D005826:Genetics, Medical; D006801:Humans; D007558:Italy; D035583:Rare Diseases / Q000235:genetics* / Q000628:therapy