title: An emerging era of clinical benefit from gene therapy.
authors.affiliation: Laboratory of Host Defenses, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Maryland.
authors.forename: Harry L
authors.initials: HL
authors.lastname: Malech
authors.affiliation: Department of Pediatrics, University of Washington and Seattle Children's Research Institute, Seattle.
authors.forename: Hans D
authors.initials: HD
authors.lastname: Ochs
mesh_terms: D015316:Genetic Therapy; D005822:Genetic Vectors; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D016086:Lentivirus; D008297:Male; D014923:Wiskott-Aldrich Syndrome / Q000628:therapy*; D051300:Wiskott-Aldrich Syndrome Protein Family / Q000235:genetics*
chemical_list: D051300:Wiskott-Aldrich Syndrome Protein Family