title: 208th ENMC International Workshop: Formation of a European Network to develop a European data sharing model and treatment guidelines for Pompe disease Naarden, The Netherlands, 26-28 September 2014.
authors.affiliation: Friedrich-Baur-Institute, Department of Neurology, Ludwig-Maximilian University, Munich, Germany.
authors.forename: Benedikt
authors.initials: B
authors.lastname: Schoser
authors.affiliation: Paris-Est Neuromuscular Center, Pitié-Salpêtrière Hospital, INSERM U974, Université Pierre et Marie Curie, Paris, France.
authors.forename: Pascal
authors.initials: P
authors.lastname: Laforêt
authors.affiliation: Centre for Lysosomal and Metabolic Diseases, Department of Pediatrics, Erasmus MC, Rotterdam, The Netherlands.
authors.forename: Michelle E
authors.initials: ME
authors.lastname: Kruijshaar
authors.affiliation: Department of Neurosciences, University of Messina, Messina, Italy.
authors.forename: Antonio
authors.initials: A
authors.lastname: Toscano
authors.affiliation: Centre for Lysosomal and Metabolic Diseases, Department of Neurology, Erasmus MC, Rotterdam, The Netherlands.
authors.forename: Pieter A
authors.initials: PA
authors.lastname: van Doorn
authors.affiliation: Centre for Lysosomal and Metabolic Diseases, Department of Pediatrics, Erasmus MC, Rotterdam, The Netherlands. Electronic address: a.vanderploeg@erasmusmc.nl.
authors.forename: Ans T
authors.initials: AT
authors.lastname: van der Ploeg
mesh_terms: D056947:Enzyme Replacement Therapy / Q000639:trends*; D006009:Glycogen Storage Disease Type II / Q000188:drug therapy* / Q000201:enzymology; D006801:Humans; D033181:Information Dissemination; D009426:Netherlands; D017410:Practice Guidelines as Topic; D016896:Treatment Outcome