title: Eculizumab (Soliris) and paroxysmal nocturnal haemoglobinuria in children. When transfusions are too frequent.
abstract: Many uncertainties; assessment based on extrapolation of adult data.
mesh_terms: D061067:Antibodies, Monoclonal, Humanized / Q000009:adverse effects*; D001803:Blood Transfusion; D006457:Hemoglobinuria, Paroxysmal / Q000188:drug therapy*; D006801:Humans
chemical_list: D061067:Antibodies, Monoclonal, Humanized; C481642:eculizumab