title: Gene therapy for GM1 gangliosidosis: challenges of translational medicine.
authors.affiliation: 1 NIHR Biomedical Research Unit, Royal Brompton Hospital, London & Imperial College, London, UK ; 2 Department of Neurology, John Radcliffe Hospital, Oxford, UK.
authors.forename: Carl
authors.initials: C
authors.lastname: Hayward
authors.affiliation: 1 NIHR Biomedical Research Unit, Royal Brompton Hospital, London & Imperial College, London, UK ; 2 Department of Neurology, John Radcliffe Hospital, Oxford, UK.
authors.forename: Hitesh C
authors.initials: HC
authors.lastname: Patel
authors.affiliation: 1 NIHR Biomedical Research Unit, Royal Brompton Hospital, London & Imperial College, London, UK ; 2 Department of Neurology, John Radcliffe Hospital, Oxford, UK.
authors.forename: Sanjay G
authors.initials: SG
authors.lastname: Manohar
authors.affiliation: 1 NIHR Biomedical Research Unit, Royal Brompton Hospital, London & Imperial College, London, UK ; 2 Department of Neurology, John Radcliffe Hospital, Oxford, UK.
authors.forename: Alexander R
authors.initials: AR
authors.lastname: Lyon