title: Gene Therapy Briefs.
authors.forename: Alex
authors.initials: A
authors.lastname: Philippidis
mesh_terms: D002318:Cardiovascular Diseases / Q000628:therapy; D015316:Genetic Therapy; D006467:Hemophilia A / Q000628:therapy; D006801:Humans; D057130:Leber Congenital Amaurosis / Q000628:therapy; D008107:Liver Diseases / Q000628:therapy; D009369:Neoplasms / Q000628:therapy; D035583:Rare Diseases / Q000628:therapy; D016896:Treatment Outcome