title: A Clinical Trial of Gene Therapy for Mucopolysaccharidosis VI, a Severe Lysosomal Storage Disorder (MeuSIX).
mesh_terms: D000818:Animals; D000229:Dependovirus / Q000235:genetics*; D015316:Genetic Therapy; D005822:Genetic Vectors; D006801:Humans; D008099:Liver; D009087:Mucopolysaccharidosis VI / Q000235:genetics / Q000378:metabolism / Q000628:therapy*; D020051:N-Acetylgalactosamine-4-Sulfatase / Q000235:genetics* / Q000378:metabolism
chemical_list: D020051:N-Acetylgalactosamine-4-Sulfatase