title: A personal perspective of orphan drug development for rare diseases: A golden opportunity or an unsustainable future?
authors.affiliation: Morris Plains, NJ, USA.
authors.forename: Charles
authors.initials: C
authors.lastname: Oo
authors.affiliation: Vince & Associates Clinical Research, Inc., Overland Park, KS, USA.
authors.forename: Lorraine M
authors.initials: LM
authors.lastname: Rusch
mesh_terms: D017277:Drug Approval / Q000191:economics* / Q000331:legislation & jurisprudence / Q000379:methods; D006801:Humans; D009965:Orphan Drug Production / Q000191:economics* / Q000331:legislation & jurisprudence; D035583:Rare Diseases / Q000188:drug therapy*; D014481:United States; D014486:United States Food and Drug Administration