title: Rare inherited diseases merit disease-specific trials.
authors: APHP, Department of Genetics, Inserm U 1127, CNRS UMR 7225, Sorbonne Universités, UPMC Univ Paris 06 UMR S 1127, Institut du Cerveau et de la Moelle Épinière, ICM, University Hospital Pitié-Salpêtrière, Paris, France. Electronic address: alexandra.durr@upmc.fr.
authors: Alexandra
authors: A
authors: Durr
mesh_terms: D018691:Excitatory Amino Acid Antagonists / Q000494:pharmacology*; D005260:Female; D005621:Friedreich Ataxia / Q000188:drug therapy*; D006801:Humans; D008297:Male; D019782:Riluzole / Q000494:pharmacology*; D020754:Spinocerebellar Ataxias / Q000188:drug therapy*
chemical_list: D018691:Excitatory Amino Acid Antagonists; D019782:Riluzole