Rare pulmonary diseases and orphan drugs: where do we stand and where are we going to?
U.O. di Pneumologia e Terapia Semi-Intensiva Respiratoria, Servizio di Fisiopatologia Respiratoria ed Emodinamica Polmonare, Ospedale San Giuseppe, MultiMedica IRCCS, Milan, Italy sharari@ilpolmone.it.
Sergio
S
Harari
Univ. Paris-Sud, Faculté de Médecine, Le Kremlin-Bicêtre, France AP-HP, Centre de Référence de l'Hypertension Pulmonaire Sévère, Département Hospitalo-Universitaire (DHU) Thorax Innovation (TORINO), Service de Pneumologie, Hôpital de Bicêtre, Le Kremlin-Bicêtre, France UMR_S 999, Univ. Paris-Sud, INSERM, Laboratoire d'Excellence (LabEx) en Recherche sur le Médicament et l'Innovation Thérapeutique (LERMIT), Centre Chirurgical Marie Lannelongue, Le Plessis-Robinson, France.
Marc
M
Humbert
Dept of Pathophysiology and Transplantation, University of Milan, IRCCS Fondazione Ospedale Maggiore, Policlinico Cà Granda, Milan, Italy.
Francesco
F
Blasi
University of California San Francisco, San Francisco, CA, USA.
Harold R
HR
Collard
Dept of Experimental and Clinical Medicine, Division of Rheumatology AOUC, School of Medicine, University of Florence, Florence, Italy.
Marco
M
Matucci-Cerinic
Univ. Paris-Sud, Faculté de Médecine, Le Kremlin-Bicêtre, France AP-HP, Centre de Référence de l'Hypertension Pulmonaire Sévère, Département Hospitalo-Universitaire (DHU) Thorax Innovation (TORINO), Service de Pneumologie, Hôpital de Bicêtre, Le Kremlin-Bicêtre, France UMR_S 999, Univ. Paris-Sud, INSERM, Laboratoire d'Excellence (LabEx) en Recherche sur le Médicament et l'Innovation Thérapeutique (LERMIT), Centre Chirurgical Marie Lannelongue, Le Plessis-Robinson, France.
Gerald
G
Simonneau
Dept of Clinical and Experimental Biomedicine, Section of Respiratory Diseases, Regional Center for Interstitial and Rare Lung Diseases, University of Catania, Policlinico "G. Rodolico", Catania, Italy.
Carlo
C
Vancheri
Royal Brompton and Harefield NHS Foundation Trust, London, UK.
Athol U
AU
Wells
Hospices Civils de Lyon, Hôpital Louis Pradel, Service de Pneumologie, Centre de Référence National des Maladies Pulmonaires Rares, Lyon, France Université de Lyon, Université Lyon I, INRA, UMR754 INRA, Vetagrosup EPHE IFR 128, Lyon, France.
Vincent
V
Cottin
D035843:Biomedical Research / Q000639:trends*; D005544:Forecasting; D006801:Humans; D008168:Lung / Q000187:drug effects* / Q000503:physiopathology; D008171:Lung Diseases / Q000175:diagnosis / Q000188:drug therapy* / Q000503:physiopathology; D009965:Orphan Drug Production; D035583:Rare Diseases / Q000175:diagnosis / Q000188:drug therapy* / Q000503:physiopathology; D019141:Respiratory System Agents / Q000627:therapeutic use*; D003226:Congresses as Topic
D019141:Respiratory System Agents