title: The Role of Patient Advocacy Organizations in Advancing Human Gene Therapy.
authors.affiliation: Editor in Chief.
authors.forename: Terence R
authors.initials: TR
authors.lastname: Flotte
mesh_terms: D015316:Genetic Therapy / Q000191:economics*; D006269:Health Facilities, Proprietary / Q000191:economics / Q000600:supply & distribution; D006801:Humans; D010344:Patient Advocacy; D019896:alpha 1-Antitrypsin Deficiency / Q000191:economics / Q000235:genetics / Q000473:pathology / Q000628:therapy*