title: A Journey in the Development of Gene Therapy for Inherited Disorders of the Bone Marrow.
authors.forename: Donald
authors.initials: D
authors.lastname: Kohn
authors.affiliation: 1 Editor, Human Gene Therapy Clinical Development, University of California , Los Angeles, California.
authors.forename: James M
authors.initials: JM
authors.lastname: Wilson
mesh_terms: D000243:Adenosine Deaminase / Q000172:deficiency* / Q000235:genetics; D000361:Agammaglobulinemia / Q000235:genetics / Q000628:therapy*; D001853:Bone Marrow / Q000276:immunology*; D015316:Genetic Therapy / Q000266:history / Q000379:methods*; D049673:History, 20th Century; D049674:History, 21st Century; D006801:Humans; D016511:Severe Combined Immunodeficiency / Q000235:genetics / Q000628:therapy*; D014481:United States
chemical_list: D000243:Adenosine Deaminase