title: Venture Philanthropy and Gene Therapy: Lessons from Adrenoleukodystrophy.
authors.affiliation: The Stop ALD Foundation , Delray Beach, Florida.
authors.forename: Rachel
authors.initials: R
authors.lastname: Salzman
mesh_terms: D000074063:ATP Binding Cassette Transporter, Subfamily D, Member 1; D018528:ATP-Binding Cassette Transporters / Q000235:genetics / Q000627:therapeutic use; D000326:Adrenoleukodystrophy / Q000235:genetics / Q000628:therapy; D005653:Fund Raising; D015316:Genetic Therapy; D006801:Humans
chemical_list: C115572:ABCD1 protein, human; D000074063:ATP Binding Cassette Transporter, Subfamily D, Member 1; D018528:ATP-Binding Cassette Transporters