title: Post-authorisation assessment of orphan drugs.
authors: Department of Internal Medicine, Division of Endocrinology and Metabolism, Academic Medical Center, Amsterdam, Netherlands. Electronic address: c.e.hollak@amc.nl.
authors: Carla E M
authors: CEM
authors: Hollak
authors: Department of Internal Medicine, Division of Endocrinology and Metabolism, Academic Medical Center, Amsterdam, Netherlands.
authors: Marieke
authors: M
authors: Biegstraaten
authors: Academic Medical Center, Amsterdam, Netherlands.
authors: Marcel
authors: M
authors: Levi
authors: Amsterdam Institute for Social Science Research, University of Amsterdam, Amsterdam, Netherlands.
authors: Rob
authors: R
authors: Hagendijk
mesh_terms: D017277:Drug Approval / Q000458:organization & administration*; D005062:European Union; D000795:Fabry Disease / Q000188:drug therapy; D006801:Humans; D009965:Orphan Drug Production; D035583:Rare Diseases / Q000188:drug therapy