title: Patient's weight can decide about spending millions on enzyme replacement therapy in MPS II.
authors.affiliation: Department of Medical Genetics, Jagiellonian University, Medical College, Krakow, Poland.
authors.forename: Miroslaw
authors.initials: M
authors.lastname: Bik-Multanowski
authors.affiliation: School of Medicine in Katowice, Department of Paediatrics and Developmental Age Neurology, Medical University of Silesia, Katowice, Poland.
authors.forename: Ewa
authors.initials: E
authors.lastname: Jamroz
authors.affiliation: Department of Pediatric Gastroenterology and Metabolism, Medical University, Poznan, Poland.
authors.forename: Lukasz
authors.initials: L
authors.lastname: Kaluzny
authors.affiliation: Department of Pediatrics, Nutrition and Metabolic Diseases, The Children's Memorial Health Institute, Warszawa, Poland.
authors.forename: Ewa
authors.initials: E
authors.lastname: Pronicka
authors.affiliation: Department of Pediatrics, Nutrition and Metabolic Diseases, The Children's Memorial Health Institute, Warszawa, Poland.
authors.forename: Dariusz
authors.initials: D
authors.lastname: Rokicki
authors.affiliation: Metabolic Department, Polish Mother's Health Memorial Institute, Lodz, Poland.
authors.forename: Ewa
authors.initials: E
authors.lastname: Starostecka
authors.affiliation: Screening Department, Institute of Mother and Child, Warszawa, Poland.
authors.forename: Jolanta
authors.initials: J
authors.lastname: Sykut-Cegielska
authors.affiliation: Department of Paediatric Endocrinology and Diabetology, Pomeranian Medical University in Szczecin, Poland.
authors.forename: Mieczyslaw
authors.initials: M
authors.lastname: Walczak
keywords: Enzyme replacement; Expensive therapies; MPS, mucopolysaccharidosis; Pediatric orphan disease; Public health; Walking test