title: Gene Therapy for Hemoglobinopathies: Tremendous Successes and Remaining Caveats.
authors.affiliation: Division of Experimental Hematology and Cancer Biology, Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
authors.forename: Punam
authors.initials: P
authors.lastname: Malik
mesh_terms: D000818:Animals; D002986:Clinical Trials as Topic; D004195:Disease Models, Animal; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors / Q000235:genetics; D006453:Hemoglobinopathies / Q000628:therapy*; D006801:Humans; D016086:Lentivirus / Q000235:genetics