title: Dream On: The Pursuit to Cure Myotubular Myopathy Born out of a Mother's Vision.
authors.affiliation: President/Cofounder, The Joshua Frase Foundation .
authors.forename: Alison Rockett
authors.initials: AR
authors.lastname: Frase
mesh_terms: D015316:Genetic Therapy / Q000266:history; D049673:History, 20th Century; D049674:History, 21st Century; D006801:Humans; D020914:Myopathies, Structural, Congenital / Q000235:genetics* / Q000266:history / Q000628:therapy*